A Retrospective Study to Characterize Participants With Propionic Acidemia
Recruiting · NCT05769621
Conditions: Propionic Acidemia
At a glance
- Research payments reported, 2025
- $81,639
- U.S. investigators named
- 7
- Sites paid
- 7
- Planned or actual enrollment
- 60
About the trial
- Sponsor
- ModernaTX, Inc.
- Dates
- Started 2023-06-16; completion 2026-09-30
- Results posted
- Not yet
This is a non-interventional, observational, global, multicenter, study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).
From ClinicalTrials.gov, last updated 2026-02-05. Full record, eligibility and contacts (opens in a new tab)
Industry funding
ModernaTX, Inc. reported $81,639 in research payments for this study in 2025 (30 payments).
Research payments usually go to hospitals, universities and research sites to run a study, not to the investigators personally. A payment is not evidence of wrongdoing.
U.S. investigators named on this study
- Walla Al-hertani, M.D. Medical Genetics · Orange, CA
- Hilary J. Vernon, M.D., PH.D. Pediatrics · Baltimore, MD
- Elizabeth G. Ames, MD, PHD Medical Genetics · Ann Arbor, MI
- Can H. Ficicioglu, M.D. Medical Genetics · Philadelphia, PA
- Kevin E. Glinton, M.D. Medical Genetics · Houston, TX
- Ashley L. Andrews, MSN, CPNP Nurse Practitioners · Salt Lake City, UT
- Emily M. Shelkowitz, MD Pediatrics · Seattle, WA
Clinicians the company named as principal investigators in its Open Payments reports.
Sites paid to run it
- Baylor College of Medicine $30,714
- Children's Hospital of Philadelphia, PA $17,951
- Johns Hopkins University $11,390
- University of Utah Hospital and Clinics, UT $8,150
- Seattle Children's Hospital, WA $6,902
- Boston Children's Hospital, MA $5,063
- University of Michigan Health System, MI $1,469
Sources: CMS Open Payments research payments (program year 2025) and ClinicalTrials.gov, U.S. National Library of Medicine.