A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
Enrolling by invitation · Phase 3 · NCT05967351
Conditions: Duchenne Muscular Dystrophy
At a glance
- Research payments reported, 2025
- $1.3M
- U.S. investigators named
- 24
- Sites paid
- 32
- Planned or actual enrollment
- 400
About the trial
- Sponsor
- Sarepta Therapeutics, Inc. (with Hoffmann-La Roche)
- Tested
- delandistrogene moxeparvovec (genetic)
- Dates
- Started 2023-09-27; completion 2033-10-31
- Results posted
- Not yet
The purpose of this study is to provide a single clinical study with a uniform approach to monitoring long-term safety and efficacy in participants who received delandistrogene moxeparvovec in a previous clinical study. No study drug will be administered as part of this study.
From ClinicalTrials.gov, last updated 2026-02-06. Full record, eligibility and contacts (opens in a new tab)
Industry funding
Sarepta Therapeutics, Inc. reported $1.3M in research payments for this study in 2025 (1,046 payments).
Research payments usually go to hospitals, universities and research sites to run a study, not to the investigators personally. A payment is not evidence of wrongdoing.
U.S. investigators named on this study
- Aravindhan Veerapandiyan, MD Child Neurology · Little Rock, AR
- Chamindra G. Laverty, M.D. Neurology · San Diego, CA
- Craig M. Mcdonald, M.D. Physical Medicine & Rehabilitation (PM&R) · Sacramento, CA
- Perry B. Shieh, MD Neurology · Los Angeles, CA
- Ana C. Tesi Rocha, MD Physical Medicine & Rehabilitation (PM&R) · Palo Alto, CA
- Susan Apkon, MD Physical Medicine & Rehabilitation (PM&R) · Aurora, CO
- Carmen E. Leon Astudillo, M.D. Pediatric Pulmonology · Gainesville, FL
- Shant J. Manoushagian, M.D. Cardiology · Fort Myers, FL
- Katherine D. Mathews, MD Physical Medicine & Rehabilitation (PM&R) · Iowa City, IA
- Nancy L. Kuntz, M.D. Child Neurology · Chicago, IL
- Bridget Mcgowan, MD Child Neurology · Chicago, IL
- Jessica Nance, MD Child Neurology · Baltimore, MD
- Partha S. Ghosh, MD Neurology · Rochester, MN
- Craig M. Zaidman, MD Child Neurology · Saint Louis, MO
- Mai K. El Mallah, MD Pediatric Pulmonology · Durham, NC
- Emma Ciafaloni, MD Neurology · Rochester, NY
- Michio Hirano, M.D. Neurology · New York, NY
- Anne M. Connolly, MD Child Neurology · Columbus, OH
- Erika L. Finanger, M.D. Child Neurology · Portland, OR
- Susan Matesanz, MD Child Neurology · Philadelphia, PA
- Susan T. Iannaccone, MD Neurology · Dallas, TX
- Russell J. Butterfield, MD/PHD Child Neurology · Salt Lake City, UT
- Crystal M. Proud, M.D. Child Neurology · Norfolk, VA
- Nancy E. Bass, MD Child Neurology · Milwaukee, WI
Clinicians the company named as principal investigators in its Open Payments reports.
Sites paid to run it
- Children's Research Institute $233,739
- Washington University $216,120
- Boston Children's Hospital, MA $92,476
- Johns Hopkins University School of Medicine $70,667
- University of California Davis Medical Center, CA $69,360
- Childrens Hospital of Wisconsin $67,071
- Ronald Reagan UCLA Medical Center, CA $57,961
- University of Utah Hospital and Clinics, UT $47,645
- University of Florida $45,529
- Strong Memorial Hospital, NY $45,476
- The Regents of the University of California $43,491
- The Research Institute at Nationwide Children's Hospital $40,281
- Children's Hospital of Philadelphia, PA $36,812
- Children's Specialty Group, PLLC $31,091
- Arkansas Childrens Research $30,678
- Ann & Robert H Lurie Childrens Hospital of Chicago, IL $29,711
- The Board of Trustees of the Leland Standford Junior $28,284
- University of California San Diego Jacobs Medical Center $24,150
- Washington University in St. Louis $22,253
- Duke University $16,713
- Stanford University $16,397
- The Trustees of Columbia University in The City of New York $16,087
- University of Iowa Hospital & Clinics, IA $12,463
- Gi Reviewers LLC $9,300
- Arkansas Childrens Hospital Research Institute $6,649
- University of Texas Southwestern Medical Center $6,080
- Ohsu Hospital and Clinics, OR $3,609
- The University of Texas Southwestern Medical Center $2,044
- Children's Hospital Colorado, CO $1,848
- Columbia University Medical Center $1,388
Sources: CMS Open Payments research payments (program year 2025) and ClinicalTrials.gov, U.S. National Library of Medicine.